GM2 gangliosidosis

MeSH: D020143ORPHA: 309152

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

MeSH Code

D020143

Orphanet Code

ORPHA:309152
GM2 gangliosidosis
MeSHD020143
OrphanetORPHA:309152
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
GM2 gangliosidosis | OrphanDrug