Goldberg-Shprintzen syndrome

MeSH: C537279ORPHA: 66629

Overview

syndrome characterized by intellectual disability, specific facial gestalt and Hirschsprung's disease (HSCR). It has material basis in homozygous mutation in the KIAA1279 gene on chromosome 10q21.1

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Goldberg-Shprintzen syndrome, sourced from HPO and Orphanet clinical annotations.

Cleft palateMicrocephalyIntellectual disabilitySpecific learning disabilityAganglionic megacolonShort staturePtosisIris colobomaHypotoniaHypospadiasBifid scrotumPointed chinHypertelorismSloping foreheadMacrotiaWide nasal bridgeSeizurePachygyriaHypoplasia of the corpus callosumVentriculomegalySparse scalp hairFinger syndactylySparse eyebrow

Classification & Codes

MeSH Code

C537279

Orphanet Code

ORPHA:66629
Goldberg-Shprintzen syndrome
MeSHC537279
OrphanetORPHA:66629
Treatments0 drug(s)
Symptoms on record23 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO