Griscelli syndrome

ORPHA: 381

Overview

autosomal recessive disease characterized by silvery gray sheen of the hair and hypopigmentation of the skin

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Griscelli syndrome, sourced from HPO and Orphanet clinical annotations.

HydrocephalusAbnormal eyelash morphologyAbnormal eyebrow morphologyNystagmusJaundiceHypopigmented skin patchesIntellectual disabilitySeizureAtaxiaHypotoniaSpasticityGlobal developmental delayReduced tendon reflexesAscitesSplenomegalyThrombocytopeniaAbnormality of neutrophilsDecreased total leukocyte countFeverPyloric stenosisEncephalocelePremature graying of hairSilver-gray hairHepatomegalyLymphadenopathyImmunodeficiencyAbnormal circulating lipid concentrationDecreased circulating immunoglobulin concentrationShort statureBone marrow hypocellularityCranial nerve paralysisIris hypopigmentationPedal edemaWhite hairHepatitisAbnormality of movement

Classification & Codes

Orphanet Code

ORPHA:381
Griscelli syndrome
OrphanetORPHA:381
Treatments0 drug(s)
Symptoms on record36 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO