Griscelli syndrome type 1

MeSH: C537301ORPHA: 79476

Overview

Griscelli syndrome characterized by silvery gray sheen of the hair, hypopigmentation of the skin and neurological impairment without immunodeficiency that has material basis in mutations in the MYO5A gene on chromosome 15q21.2

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Griscelli syndrome type 1, sourced from HPO and Orphanet clinical annotations.

RetinopathyNystagmusDiplopiaIntellectual disabilitySeizureAtaxiaGlobal developmental delayHypertoniaGeneralized hypotoniaPremature graying of hairCerebral calcificationHyperlipidemiaPartial albinismIris hypopigmentationWhite hairAbnormality of movement

Classification & Codes

MeSH Code

C537301

Orphanet Code

ORPHA:79476
Griscelli syndrome type 1
MeSHC537301
OrphanetORPHA:79476
Treatments0 drug(s)
Symptoms on record16 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO