growth hormone insensitivity syndrome

ORPHA: 1813931 Treatment Available

Overview

group of hereditary diseases

Available Treatments (1)

DrugFormStatusCountriesLead Time
Somatropin
Orphan Cold Chain
InjectionFDA Approved414d

Classification & Codes

Orphanet Code

ORPHA:181393
growth hormone insensitivity syndrome
OrphanetORPHA:181393
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO