hemoglobin C-beta-thalassemia syndrome

ORPHA: 231242

Overview

Hemoglobin C - beta-thalassemia (HbC - BT) is a form of beta-thalassemia (see this term) resulting in moderate hemolytic anemia

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with hemoglobin C-beta-thalassemia syndrome, sourced from HPO and Orphanet clinical annotations.

SplenomegalyAnemiaMicrocytic anemiaAbnormal hemoglobin

Classification & Codes

Orphanet Code

ORPHA:231242
hemoglobin C-beta-thalassemia syndrome
OrphanetORPHA:231242
Treatments0 drug(s)
Symptoms on record4 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO