hereditary gelsolin amyloidosis

ORPHA: 85448

Overview

Human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with hereditary gelsolin amyloidosis, sourced from HPO and Orphanet clinical annotations.

Abnormality of the eyeDry skinDermatological manifestations of systemic disordersKeratoconjunctivitis siccaLattice corneal dystrophyBilateral ptosisXerostomiaHearing impairmentVisual impairmentCataractAbnormality of the nervous systemEdemaCutis laxaBruising susceptibilityAtaxiaPolyneuropathyDysphagiaMyokymiaDistal peripheral sensory neuropathyReduced visual acuityFacial palsyRegional abnormality of skinArrhythmiaConstrictive median neuropathyCorneal ulcerationProteinuriaGlaucomaOphthalmoparesisSensory neuropathyPruritusDysarthriaCardiomyopathyOrthostatic hypotension due to autonomic dysfunctionDiffuse skin atrophySparse hairSleep apneaBlepharochalasisTongue atrophyAbnormal spleen morphologyDepressionBulbar signsDeficit in phonologic short-term memoryStage 5 chronic kidney diseaseNail dystrophyRespiratory tract infection

Classification & Codes

Orphanet Code

ORPHA:85448
hereditary gelsolin amyloidosis
OrphanetORPHA:85448
Treatments0 drug(s)
Symptoms on record45 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO