hereditary spastic paraplegia 46

ORPHA: 320391

Overview

gene (9p13.2) encoding non-lysosomal glucosylceramidase.

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with hereditary spastic paraplegia 46, sourced from HPO and Orphanet clinical annotations.

CataractAtaxiaGait disturbanceLower limb spasticityBabinski signCerebellar atrophyCerebral atrophyCerebral cortical atrophyAbnormal cerebral white matter morphologyCorpus callosum atrophyCognitive impairmentUrinary incontinenceHearing impairmentNystagmusDementiaInfertilityHyperreflexiaPes cavusTruncal ataxiaBroad-based gaitHead tremorSpastic dysarthriaScoliosisPeripheral axonal neuropathyImpaired vibration sensation at anklesUpper limb spasticityAbnormal pyramidal signJerky ocular pursuit movementsDecreased testicular sizeReduced sperm motilityAbnormal sperm morphologyAbnormal sperm head morphologyAbnormal tendon morphology

Classification & Codes

Orphanet Code

ORPHA:320391
hereditary spastic paraplegia 46
OrphanetORPHA:320391
Treatments0 drug(s)
Symptoms on record33 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO