Hermansky-Pudlak syndrome 8

ORPHA: 231537

Overview

Hermansky-Pudlak syndrome that has material basis in homozygous mutation in the BLOC1S3 gene on chromosome 19q13

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Classification & Codes

Orphanet Code

ORPHA:231537
Hermansky-Pudlak syndrome 8
OrphanetORPHA:231537
Treatments0 drug(s)
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
Hermansky-Pudlak syndrome 8 | OrphanDrug