Hermansky-Pudlak syndrome with pulmonary fibrosis
ORPHA: 2315001 Treatment Available
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| ruxolitinib Orphan | Oral tablet, 5mg, 10mg, 15mg, 20mg, 25mg; Topical cream 1.5% | FDA Approved | 11 | 7d |
Classification & Codes
Orphanet Code
ORPHA:231500Hermansky-Pudlak syndrome with pulmonary fibrosis
| Orphanet | ORPHA:231500 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO