Hirschsprung disease-ganglioneuroblastoma syndrome

MeSH: C538119ORPHA: 2151

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Hirschsprung disease-ganglioneuroblastoma syndrome, sourced from HPO and Orphanet clinical annotations.

Abnormal pupil morphologyHyperhidrosisSeizureProlonged QT intervalAganglionic megacolonNeoplasm of the nervous systemGanglioneuroblastomaArrhythmia

Classification & Codes

MeSH Code

C538119

Orphanet Code

ORPHA:2151
Hirschsprung disease-ganglioneuroblastoma syndrome
MeSHC538119
OrphanetORPHA:2151
Treatments0 drug(s)
Symptoms on record8 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
Hirschsprung disease-ganglioneuroblastoma syndrome | OrphanDrug