holocarboxylase synthetase deficiency

MeSH: D028922ORPHA: 79242

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with holocarboxylase synthetase deficiency, sourced from HPO and Orphanet clinical annotations.

IrritabilityKeratoconjunctivitisSeizureHypotoniaGrowth delayWeight lossNausea and vomitingAnorexiaPerioral eczemaHyperammonemiaOrganic aciduriaRespiratory distressTachypneaEczematoid dermatitisAtaxiaLethargyComaAlopeciaThrombocytopeniaDesquamation of skin soon after birth

Classification & Codes

MeSH Code

D028922

Orphanet Code

ORPHA:79242
holocarboxylase synthetase deficiency
MeSHD028922
OrphanetORPHA:79242
Treatments0 drug(s)
Symptoms on record20 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO