homocystinuria without methylmalonic aciduria

ORPHA: 622

Overview

v1)

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with homocystinuria without methylmalonic aciduria, sourced from HPO and Orphanet clinical annotations.

Visual impairmentNystagmusPsychosisDementiaSeizureAtaxiaHypotoniaLethargyGlobal developmental delayFailure to thriveMegaloblastic bone marrowVomitingCerebral cortical atrophy

Classification & Codes

Orphanet Code

ORPHA:622
homocystinuria without methylmalonic aciduria
OrphanetORPHA:622
Treatments0 drug(s)
Symptoms on record13 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO