Hoyeraal-Hreidarsson syndrome

ICD-10: D61.0MeSH: C536068ORPHA: 3322

Overview

a rare multisystem disease characterized by intrauterine growth retardation, microcephaly, cerebellar hypoplasia, progressive combined immune deficiency and aplastic anemia.

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Hoyeraal-Hreidarsson syndrome, sourced from HPO and Orphanet clinical annotations.

MicrocephalyIntellectual disabilityAtaxiaGlobal developmental delayHyporeflexiaHypertoniaCerebellar hypoplasiaFailure to thriveIntrauterine growth retardationThrombocytopeniaAbnormal leukocyte morphologyAnemiaAbnormality of coagulationVentriculomegalyCerebral cortical atrophySparse scalp hairPremature graying of hairCerebral calcificationNeoplasmImmunodeficiencyOral leukoplakiaShort statureDermal atrophyBone marrow hypocellularityExcessive wrinkled skinGeneralized hyperpigmentationNail dystrophyGeneralized hypopigmentation of hair

Classification & Codes

ICD-10 Code

D61.0

MeSH Code

C536068

Orphanet Code

ORPHA:3322
Hoyeraal-Hreidarsson syndrome
ICD-10D61.0
MeSHC536068
OrphanetORPHA:3322
Treatments0 drug(s)
Symptoms on record28 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO