Hurler syndrome

ORPHA: 93473

Overview

genetic disorder that results in the buildup of glycosaminoglycans (AKA GAGs, or mucopolysaccharides) due to a deficiency of alpha-L iduronidase

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Hurler syndrome, sourced from HPO and Orphanet clinical annotations.

MacroglossiaEverted lower lip vermilionHydrocephalusDolichocephalyCoarse facial featuresFull cheeksHearing impairmentWide nasal bridgeAnteverted naresShort neckRetinopathyGlaucomaThick eyebrowDepressionAbnormal rib morphologyHypertensionAbnormal clavicle morphologyAbnormality of the skeletal systemAbnormal diaphysis morphologyAbnormality of skin pigmentationIntellectual disabilityHypotoniaGlobal developmental delayLimitation of joint mobilityGrowth delayCardiomyopathyAbnormal heart valve morphologyAngina pectorisEndocardial fibroelastosisSplenomegalyFrontal bossingChronic diarrheaRecurrent respiratory infectionsGeneralized hirsutismHepatomegalySpastic paraparesisSleep disturbanceScoliosisSkeletal dysplasiaNarrow pelvis boneSpinal canal stenosisAbnormal vertebral morphologyShort statureDepressed nasal bridgeAbnormal epiphysis morphologyAbnormal pyramidal signCorneal opacityMucopolysacchariduriaAbnormality of the elbowFeeding difficultiesRhinitisThick vermilion borderAbnormal nerve conduction velocityCerebral palsyCamptodactyly of fingerLarge faceAbnormality of the tonsilsHernia

Classification & Codes

Orphanet Code

ORPHA:93473
Hurler syndrome
OrphanetORPHA:93473
Treatments0 drug(s)
Symptoms on record58 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
Hurler syndrome | OrphanDrug