hyperprolinemia type 2

ORPHA: 79101

Overview

hyperprolinemia that has material basis in homozygous or compound heterozygous mutation in the pyrroline-5-carboxylate dehydrogenase gene on chromosome 1p36

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with hyperprolinemia type 2, sourced from HPO and Orphanet clinical annotations.

Atypical behaviorIntellectual disabilitySeizureGlobal developmental delayAbnormal cerebrospinal fluid morphologyHydroxyprolinuriaProlinuriaHyperprolinemiaAbnormal circulating enzyme concentration or activityIncreased urine alpha-ketoglutarate concentrationDelayed speech and language developmentHyperglycinemiaGeneralized-onset seizureUnsteady gaitSleep disturbanceIncreased CSF protein concentrationHyperalaninemiaMuscle spasmExercise intoleranceReduced circulating vitamin B6 circulatingEEG with generalized sharp slow wavesChronic fatigueRenal insufficiencyAbnormality of eye movementVertical supranuclear gaze palsyOphthalmoparesisDepressionAggressive behaviorAutistic behaviorShort attention spanHallucinationsAnxietyAreflexiaConfusionEncephalopathyPsychotic mentationDiarrheaDysphagiaAbdominal painStatus epilepticusFebrile seizure (within the age range of 3 months to 6 years)Increased CSF lactateDistal sensory impairmentMyalgiaSpeech articulation difficultiesPeripheral neuropathyAtonic seizureEarly onset absence seizuresMild global developmental delayFeeding difficultiesDysesthesia

Classification & Codes

Orphanet Code

ORPHA:79101
hyperprolinemia type 2
OrphanetORPHA:79101
Treatments0 drug(s)
Symptoms on record51 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO