hypertrophic cardiomyopathy and renal tubular disease due to mitochondrial DNA mutation

ORPHA: 324525

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with hypertrophic cardiomyopathy and renal tubular disease due to mitochondrial DNA mutation, sourced from HPO and Orphanet clinical annotations.

Global developmental delayFailure to thriveIntrauterine growth retardationCardiomyopathyCerebral atrophyRespiratory insufficiencyIncreased circulating lactate concentrationElevated circulating creatine kinase concentrationFeeding difficulties in infancyFloppy infantDecreased activity of mitochondrial complex IChronic kidney diseaseSeizureRenal tubular acidosisIncreased CSF lactateHypsarrhythmiaHyperalaninemia3-Methylglutaconic aciduriaShort statureDecreased activity of mitochondrial complex III

Classification & Codes

Orphanet Code

ORPHA:324525
hypertrophic cardiomyopathy and renal tubular disease due to mitochondrial DNA mutation
OrphanetORPHA:324525
Treatments0 drug(s)
Symptoms on record20 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
hypertrophic cardiomyopathy and renal tubular disease due to mitochondrial DNA mutation | OrphanDrug