immunodeficiency 55
ORPHA: 5052272 Treatments Available
Overview
human disease
Available Treatments (2)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| Berotralstat Orphan | Capsule | FDA Approved | 4 | 14d |
| C1 esterase inhibitor (human) Orphan Cold Chain | Lyophilized powder for reconstitution | FDA Approved | 4 | 7d |
Classification & Codes
Orphanet Code
ORPHA:505227immunodeficiency 55
| Orphanet | ORPHA:505227 |
| Treatments | 2 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO