immunodeficiency due to a genetic complement cascade protein anomaly
ORPHA: 1019921 Treatment Available
Overview
human disease
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| Ravulizumab Orphan Cold Chain | IV infusion | FDA Approved | 4 | — |
Classification & Codes
Orphanet Code
ORPHA:101992immunodeficiency due to a genetic complement cascade protein anomaly
| Orphanet | ORPHA:101992 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO