infantile osteopetrosis with neuroaxonal dysplasia

MeSH: C536055ORPHA: 85179

Overview

This syndrome is characterized by osteopetrosis, agenesis of the corpus callosum, cerebral atrophy and a small hippocampus

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with infantile osteopetrosis with neuroaxonal dysplasia, sourced from HPO and Orphanet clinical annotations.

SeizureGlobal developmental delayAgenesis of corpus callosumPartial agenesis of the corpus callosumCerebral atrophyVentriculomegalyIncreased skull ossificationCranial nerve paralysisPeripheral neuropathyBrain atrophyAbnormal myelinationHypoplastic hippocampusConductive hearing impairmentPneumoniaFetal distress

Classification & Codes

MeSH Code

C536055

Orphanet Code

ORPHA:85179
infantile osteopetrosis with neuroaxonal dysplasia
MeSHC536055
OrphanetORPHA:85179
Treatments0 drug(s)
Symptoms on record15 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO