isolated partial cerebellar vermis agenesis

ORPHA: 2692091 Treatment Available

Overview

human disease

Available Treatments (1)

DrugFormStatusCountriesLead Time
Vigabatrin
Orphan
Oral tablet 500mg; Oral powder for solution 500mg sachetsFDA Approved, EMA Approved614d

Classification & Codes

Orphanet Code

ORPHA:269209
isolated partial cerebellar vermis agenesis
OrphanetORPHA:269209
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
isolated partial cerebellar vermis agenesis | OrphanDrug