isolated unilateral hemispheric cerebellar hypoplasia

ORPHA: 2692182 Treatments Available

Overview

human disease

Available Treatments (2)

DrugFormStatusCountriesLead Time
carbamazepine
oral tablet 200mg, 400mg; extended-release tablet; oral suspension 100mg/5mLFDA Approved117d
Baclofen
Oral tablets 10mg, 20mg; Intrathecal injection 0.05mg/mL, 10mg/20mLFDA Approved77d

Classification & Codes

Orphanet Code

ORPHA:269218
isolated unilateral hemispheric cerebellar hypoplasia
OrphanetORPHA:269218
Treatments2 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO