Krabbe disease

MeSH: D007965ORPHA: 487

Overview

congenital disorder of the nervous system

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Krabbe disease, sourced from HPO and Orphanet clinical annotations.

Hearing impairmentSensorineural hearing impairmentVisual impairmentAtypical behaviorSensory neuropathyAbnormal thumb morphologyAtaxiaSpasticityGlobal developmental delayAbnormality of metabolism/homeostasisCloverleaf skullEMG abnormalityPeripheral neuropathyAplasia/Hypoplasia of the abdominal wall musculatureFeeding difficultiesReduced tissue galactocerebrosidase activityIrritabilitySeizureGait disturbanceFailure to thriveFeverVomitingGeneralized myoclonic seizureRecurrent respiratory infectionsSpastic paraparesisDevelopmental regressionAbnormality of peripheral nerve conductionHemiplegia/hemiparesisHyperpyrexiaUrinary incontinenceBlindnessOptic atrophyHand clenchingHyporeflexiaMuscle weaknessMyoclonusPes cavusWeight lossOpisthotonusClumsinessFrequent fallsPoor head controlTetraplegiaRespiratory failureIncreased CSF protein concentrationDecerebrate rigiditySlow pupillary light responseErectile dysfunctionHyperesthesia

Classification & Codes

MeSH Code

D007965

Orphanet Code

ORPHA:487
Krabbe disease
MeSHD007965
OrphanetORPHA:487
Treatments0 drug(s)
Symptoms on record49 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO