LEOPARD syndrome

MeSH: D044542ORPHA: 500

Overview

rare autosomal dominant,[3] multisystem disease caused by a mutation in the protein tyrosine phosphatase, non-receptor type 11 gene (PTPN11)

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with LEOPARD syndrome, sourced from HPO and Orphanet clinical annotations.

Abnormality of the genital systemHypertelorismSensorineural hearing impairmentHyperextensible skinMelanocytic nevusMultiple lentiginesFrecklingGrowth delayIntrauterine growth retardationHypertrophic cardiomyopathyAbnormal pulmonary valve morphologyPulmonic stenosisAbnormality of the pulmonary arterySevere sensorineural hearing impairmentArrhythmiaBundle branch blockCryptorchidismDecreased fertilityAbnormality of the faceWide nasal bridgeWebbed neckPtosisPectus excavatumPectus carinatumSprengel anomalyAbnormal mitral valve morphologyMitral valve prolapseScapular wingingShort statureAtrioventricular canal defectAbnormal cardiovascular system morphologyHypospadiasBrachycephalyTriangular faceMild intellectual disabilityGlobal developmental delaySubcutaneous noduleAbnormality of the voiceMyocardial infarctionVascular dilatationScoliosisMelanomaMyelodysplasiaNeuroblastomaSpina bifida occultaAbnormal endocardium morphologyExcessive wrinkled skinAplasia/Hypoplasia of the abdominal wall musculatureAbnormal localization of kidneyPosteriorly rotated ears

Classification & Codes

MeSH Code

D044542

Orphanet Code

ORPHA:500
LEOPARD syndrome
MeSHD044542
OrphanetORPHA:500
Treatments0 drug(s)
Symptoms on record50 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO