lethal Kniest-like dysplasia

MeSH: C537208ORPHA: 2347

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with lethal Kniest-like dysplasia, sourced from HPO and Orphanet clinical annotations.

Cleft palateMacrocephalyWide anterior fontanelLow-set earsShort neckShort ribsNarrow chestAnterior rib cuppingPlatyspondylyHypoplastic iliaEdemaBrachydactylyProtuberant abdomenPolyhydramniosBreech presentationAtrial septal defectTalipes equinovarusAbnormal cartilage morphologyFlared metaphysisAbnormal ischium morphologyCoronal cleft vertebraeMesomelic/rhizomelic limb shorteningBroad long bonesAbnormal cartilage matrixHypoplastic vertebral bodiesSevere short-limb dwarfismFlat face

Classification & Codes

MeSH Code

C537208

Orphanet Code

ORPHA:2347
lethal Kniest-like dysplasia
MeSHC537208
OrphanetORPHA:2347
Treatments0 drug(s)
Symptoms on record27 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO