limb-girdle muscular dystrophy

MeSH: D049288ORPHA: 2631 Treatment Available

Overview

muscular dystrophy characterized by weakening of the muscles of the hip and shoulders which comprise the limb girdle muscles

Available Treatments (1)

DrugFormStatusCountriesLead Time
Deflazacort
Orphan
Oral tablet, Oral suspensionFDA Approved27d

Classification & Codes

MeSH Code

D049288

Orphanet Code

ORPHA:263
limb-girdle muscular dystrophy
MeSHD049288
OrphanetORPHA:263
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
limb-girdle muscular dystrophy | OrphanDrug