lissencephaly due to LIS1 mutation

ORPHA: 95232

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with lissencephaly due to LIS1 mutation, sourced from HPO and Orphanet clinical annotations.

SeizureThick cerebral cortexInfantile spasmsProgressive microcephalyAbnormal corpus callosum morphologyPachygyriaHypoplasia of the corpus callosumVentriculomegalyCavum septum pellucidumPoor head controlTetraplegiaLanguage impairmentImpaired smooth pursuitAxial hypotoniaEEG with spike-wave complexesSevere intellectual disabilityFeeding difficultiesDilation of Virchow-Robin spacesNeurodevelopmental delayAnterior predominant thick cortex pachygyriaDelayed ability to sitAgyriaDysgyriaEpileptic encephalopathyMild intellectual disabilityNeonatal hypotoniaPolyhydramniosGeneralized myoclonic seizureOpisthotonusProfound intellectual disabilityDevelopmental regressionFocal impaired awareness seizureHypsarrhythmiaNeonatal hyperbilirubinemiaAtypical absence seizureGeneralized tonic seizureAtonic seizureFocal motor seizureEEG with changes in voltageAspiration pneumoniaPosterior predominant thick cortex pachygyriaCerebellar vermis hypoplasiaProgressive spastic quadriplegiaScoliosis

Classification & Codes

Orphanet Code

ORPHA:95232
lissencephaly due to LIS1 mutation
OrphanetORPHA:95232
Treatments0 drug(s)
Symptoms on record44 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
lissencephaly due to LIS1 mutation | OrphanDrug