Machado-Joseph disease

ICD-10: G11.1MeSH: D017827ORPHA: 98757

Overview

autosomal dominant cerebellar ataxia that is characterized by slow degeneration of the hindbrain and has material basis in expansion of CAG triplet repeats (glutamine) in the ATXN3 gene

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Machado-Joseph disease, sourced from HPO and Orphanet clinical annotations.

ProptosisProgressive external ophthalmoplegiaNystagmusDiplopiaDelayed speech and language developmentDysarthriaDystoniaHyperreflexiaAbnormality of extrapyramidal motor functionProgressive cerebellar ataxiaClumsinessSkeletal muscle atrophyAbnormal pyramidal signVocal cord paralysisAbnormal vestibular functionAbnormality of temperature regulation

Classification & Codes

ICD-10 Code

G11.1

MeSH Code

D017827

Orphanet Code

ORPHA:98757
Machado-Joseph disease
ICD-10G11.1
MeSHD017827
OrphanetORPHA:98757
Treatments0 drug(s)
Symptoms on record16 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO