medium chain acyl-CoA dehydrogenase deficiency

ICD-10: E71.311MeSH: C536038ORPHA: 42

Overview

lipid metabolism disorder that is characterized by a deficiency of the enzyme medium chain acyl-CoA dehydrogenase that results in the inability to convert medium chain fatty acids to energy, particularly during fasting

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with medium chain acyl-CoA dehydrogenase deficiency, sourced from HPO and Orphanet clinical annotations.

HypotoniaReduced tendon reflexesDecreased liver functionHyperammonemiaVomitingHepatomegalyDicarboxylic aciduriaFatigable weaknessProximal muscle weaknessExercise-induced myalgiaDecreased plasma total carnitineFatigable weakness of neck musclesMacrocephalyDelayed speech and language developmentAtaxiaLethargyComaHepatic steatosisCardiomegalyHypoglycemiaKetosisDiarrheaBilateral tonic-clonic seizureFebrile seizure (within the age range of 3 months to 6 years)Exertional dyspneaElevated circulating hepatic transaminase concentrationMyopathySkeletal muscle atrophyElevated circulating creatine kinase concentrationMuscle spasmCachexiaDistal arthrogryposisLoss of consciousnessArrhythmiaFatigueElevated urinary 3-hydroxybutyric acidAbnormal circulating lactate dehydrogenase concentration

Classification & Codes

ICD-10 Code

E71.311

MeSH Code

C536038

Orphanet Code

ORPHA:42
medium chain acyl-CoA dehydrogenase deficiency
ICD-10E71.311
MeSHC536038
OrphanetORPHA:42
Treatments0 drug(s)
Symptoms on record37 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
medium chain acyl-CoA dehydrogenase deficiency | OrphanDrug