methylcobalamin deficiency type cblE

MeSH: C565510ORPHA: 2169

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with methylcobalamin deficiency type cblE, sourced from HPO and Orphanet clinical annotations.

Global developmental delayMegaloblastic bone marrowHyperhomocystinemiaMicrocephalyAbnormality of the eyeIntellectual disabilitySeizureHypotoniaFailure to thriveIntrauterine growth retardationMacrocytic anemiaVomitingAbnormal speech patternDrowsinessAbnormal cerebral white matter morphologyHypomethioninemiaIncreased mean corpuscular volumeLoss of consciousnessPostnatal growth retardationSevere global developmental delayFeeding difficultiesBrain atrophyAbnormality of movementHydrocephalusHearing impairmentVisual impairmentNystagmusAtypical behaviorHypertensionAbnormality of the skeletal systemOsteoporosisSyndactylyLethargyExcessive daytime somnolenceAbnormality of the liverAbnormality of the cardiovascular systemDecreased total neutrophil countPancytopeniaThromboembolismVentriculomegalyHypoplasia of the brainstemDeep venous thrombosisScoliosisHemolytic-uremic syndromeLower limb hypertoniaPeripheral neuropathyDelayed myelinationWidened subarachnoid spaceClinodactylyGlomerulopathy

Classification & Codes

MeSH Code

C565510

Orphanet Code

ORPHA:2169
methylcobalamin deficiency type cblE
MeSHC565510
OrphanetORPHA:2169
Treatments0 drug(s)
Symptoms on record50 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO