methylmalonic acidemia with homocystinuria, type cblX

MeSH: C563136ORPHA: 3699621 Treatment Available

Overview

human disease

Available Treatments (1)

DrugFormStatusCountriesLead Time
Vitamin B12 (Cobalamin)
Injection, oral tablet4

Classification & Codes

MeSH Code

C563136

Orphanet Code

ORPHA:369962
methylmalonic acidemia with homocystinuria, type cblX
MeSHC563136
OrphanetORPHA:369962
Treatments1 drug(s)
Statuspublished

Treatment Summary

Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO