microcephaly-seizures-intellectual disability-heart disease syndrome

MeSH: C537544ORPHA: 2519

Overview

Microcephaly-seizures-intellectual disability-heart disease syndrome is characterised by intellectual deficit, a cardiac anomaly, micropenis, hypothyroidism, epileptic seizures, and skeletal anomalies. It has been described in two males.

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with microcephaly-seizures-intellectual disability-heart disease syndrome, sourced from HPO and Orphanet clinical annotations.

MicropenisCongenital hypothyroidismIntellectual disabilitySeizureGlobal developmental delayAtrial septal defectCongenital nystagmusFloppy infantCryptorchidismMicrocephalyEpicanthusEsotropiaAbnormal sternum morphologyAbnormal rib morphologyShort ribsBroad ribsPostaxial hand polydactylyVentricular septal defectPatent ductus arteriosusHypoplasia of the corpus callosumPulmonary arterial hypertensionRespiratory distressSupernumerary nippleRedundant neck skin

Classification & Codes

MeSH Code

C537544

Orphanet Code

ORPHA:2519
microcephaly-seizures-intellectual disability-heart disease syndrome
MeSHC537544
OrphanetORPHA:2519
Treatments0 drug(s)
Symptoms on record24 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO