microphthalmia-brain atrophy syndrome

MeSH: C566985ORPHA: 77299

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with microphthalmia-brain atrophy syndrome, sourced from HPO and Orphanet clinical annotations.

BlindnessBilateral microphthalmosMicrocephalySpasticityVomitingDevelopmental regressionDiffuse cerebral atrophyLateral ventricle dilatationDiffuse demyelination of the cerebral white matterAtrophy/Degeneration affecting the brainstemCorpus callosum atrophyInappropriate cryingMultifocal seizuresGeneralized myoclonic seizureGeneralized-onset seizureCerebellar vermis atrophyAbnormal pons morphologyFocal hyperkinetic seizureVegetative stateTongue thrusting

Classification & Codes

MeSH Code

C566985

Orphanet Code

ORPHA:77299
microphthalmia-brain atrophy syndrome
MeSHC566985
OrphanetORPHA:77299
Treatments0 drug(s)
Symptoms on record20 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO