mitochondrial complex I deficiency

MeSH: C537475ORPHA: 2609

Overview

Human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with mitochondrial complex I deficiency, sourced from HPO and Orphanet clinical annotations.

Decreased activity of mitochondrial complex IProximal tubulopathySensorineural hearing impairmentStrabismusPtosisOptic disc pallorNystagmusReduced eye contactOptic neuropathyAtaxiaHypotoniaLethargyGlobal developmental delayEncephalopathyMuscle weaknessFailure to thriveIntrauterine growth retardationHypertrophic cardiomyopathyHypoglycemiaVomitingRespiratory insufficiencyHepatomegalyLeukoencephalopathyLeukodystrophyPoor head controlIncreased CSF lactateLactic acidosisIncreased circulating pyruvate concentrationMitochondrial myopathyParoxysmal involuntary eye movementsAbnormal mitochondria in muscle tissueFocal T2 hyperintense brainstem lesionMicrocephalyBlindnessDiabetes mellitusFeeding difficultiesFetal distress

Classification & Codes

MeSH Code

C537475

Orphanet Code

ORPHA:2609
mitochondrial complex I deficiency
MeSHC537475
OrphanetORPHA:2609
Treatments0 drug(s)
Symptoms on record37 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO