mitochondrial DNA depletion syndrome 12b

ORPHA: 1369

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with mitochondrial DNA depletion syndrome 12b, sourced from HPO and Orphanet clinical annotations.

StrabismusGlaucomaAbnormal electroretinogramCataractMyopiaNystagmusCorneal dystrophyHypertrophic cardiomyopathyLactic acidosisMyopathy

Classification & Codes

Orphanet Code

ORPHA:1369
mitochondrial DNA depletion syndrome 12b
OrphanetORPHA:1369
Treatments0 drug(s)
Symptoms on record10 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
mitochondrial DNA depletion syndrome 12b | OrphanDrug