mitochondrial DNA depletion syndrome 2

MeSH: C563698ORPHA: 254875

Overview

Human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with mitochondrial DNA depletion syndrome 2, sourced from HPO and Orphanet clinical annotations.

MyopathyGeneralized hypotoniaMuscle weaknessRespiratory insufficiencyMotor deteriorationHypotoniaHyporeflexiaMotor delayGait disturbanceFailure to thrive in infancyRespiratory distressGeneralized-onset seizureDevelopmental regressionDistal muscle weaknessRespiratory insufficiency due to muscle weaknessRespiratory failureSkeletal muscle atrophyGeneralized muscle weaknessExercise intoleranceDifficulty standingRecurrent pneumoniaInfantile encephalopathyFeeding difficulties in infancyProgressive proximal muscle weaknessChronic fatigueProgressive external ophthalmoplegiaOphthalmoparesisDysarthriaBulbar palsyBilateral ptosisDysphagiaMyalgiaVentilator dependence with inability to weanInfantile sensorineural hearing impairmentSevere sensorineural hearing impairmentWeakness of facial musculatureCognitive impairmentScoliosisSpinal muscular atrophy

Classification & Codes

MeSH Code

C563698

Orphanet Code

ORPHA:254875
mitochondrial DNA depletion syndrome 2
MeSHC563698
OrphanetORPHA:254875
Treatments0 drug(s)
Symptoms on record39 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO