mitochondrial DNA depletion syndrome 5

MeSH: C567624ORPHA: 1933

Overview

Human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with mitochondrial DNA depletion syndrome 5, sourced from HPO and Orphanet clinical annotations.

MicrocephalySensorineural hearing impairmentVisual impairmentPtosisAbnormal electroretinogramAbnormality of visual evoked potentialsAtypical behaviorDecreased nerve conduction velocitySeizureAtaxiaGlobal developmental delayHyporeflexiaVentriculomegalyDelayed gross motor developmentGeneralized hirsutismCerebral calcificationSkeletal muscle atrophyElevated circulating creatine kinase concentrationAminoaciduriaShort statureCachexiaIntellectual disabilityMethylmalonic aciduria

Classification & Codes

MeSH Code

C567624

Orphanet Code

ORPHA:1933
mitochondrial DNA depletion syndrome 5
MeSHC567624
OrphanetORPHA:1933
Treatments0 drug(s)
Symptoms on record23 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO