muscle-eye-brain disease

ORPHA: 588

Overview

disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with muscle-eye-brain disease, sourced from HPO and Orphanet clinical annotations.

HydrocephalusStrabismusGlaucomaVisual impairmentCataractMyopiaOptic atrophySeizureHypotoniaHypertoniaGait disturbanceHoloprosencephalyAbnormality of the voiceAbnormal speech patternEEG abnormalityMeningoceleMyopathyElevated circulating creatine kinase concentrationEMG abnormalityHemiplegia/hemiparesisAplasia/Hypoplasia of the cerebellumAbnormality of movementCognitive impairment

Classification & Codes

Orphanet Code

ORPHA:588
muscle-eye-brain disease
OrphanetORPHA:588
Treatments0 drug(s)
Symptoms on record23 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO