myofibrillar myopathy 2

MeSH: C563848ORPHA: 399058

Overview

Human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with myofibrillar myopathy 2, sourced from HPO and Orphanet clinical annotations.

DysphoniaDysphagiaProgressive distal muscle weaknessNeck muscle weaknessHyporeflexiaLimb-girdle muscle weaknessAxial muscle weaknessEMG: myopathic abnormalitiesIncreased variability in muscle fiber diameterAutophagic vacuolesFoot dorsiflexor weaknessAccumulation of muscle fiber desminAbnormal circulating creatine kinase concentrationPosterior capsular cataractMuscle fiber inclusion bodiesGait disturbanceFacial diplegiaCardiomyopathyRespiratory insufficiency due to muscle weaknessMuscle stiffnessProgressive proximal muscle weakness

Classification & Codes

MeSH Code

C563848

Orphanet Code

ORPHA:399058
myofibrillar myopathy 2
MeSHC563848
OrphanetORPHA:399058
Treatments0 drug(s)
Symptoms on record21 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
myofibrillar myopathy 2 | OrphanDrug