nemaline myopathy
MeSH: D017696ORPHA: 607
Overview
congenital structural myopathy characterized by generally non-progressive muscle weakness of varying severity
Available Treatments (0)
No treatments linked yet
Clinical trials or compassionate use may be available — consult a specialist.
Classification & Codes
MeSH Code
D017696Orphanet Code
ORPHA:607nemaline myopathy
| MeSH | D017696 |
| Orphanet | ORPHA:607 |
| Treatments | 0 drug(s) |
| Status | published |
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO