Neonatal adrenoleukodystrophy

ORPHA: 44

Overview

medical condition

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with Neonatal adrenoleukodystrophy, sourced from HPO and Orphanet clinical annotations.

Sensorineural hearing impairmentWide nasal bridgeAbnormal palate morphologyDolichocephalyHigh foreheadAnteverted naresStrabismusNystagmusOptic atrophySeizureHypotoniaHyperreflexiaAbnormality of the liverAbnormality of metabolism/homeostasisEEG abnormalityDevelopmental regressionShort staturePrimary adrenal insufficiencySevere global developmental delayAbnormality of movementMacrocephalyWide anterior fontanelVisual impairmentPtosisCataractAbnormality of neuronal migrationBilateral single transverse palmar creasesAbnormal retinal pigmentationPosteriorly rotated ears

Classification & Codes

Orphanet Code

ORPHA:44
Neonatal adrenoleukodystrophy
OrphanetORPHA:44
Treatments0 drug(s)
Symptoms on record29 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO