nephropathic infantile cystinosis

ORPHA: 411629

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with nephropathic infantile cystinosis, sourced from HPO and Orphanet clinical annotations.

Renal tubular dysfunctionCorneal crystalsPhotophobiaFailure to thriveGrowth delayAcidosisDehydrationPolydipsiaAbnormal tubulointerstitial morphologyRenal Fanconi syndromeVomitingConstipationHypophosphatemiaRicketsHypokalemiaGlycosuriaHyperphosphaturiaAbnormal blood ion concentrationLow-molecular-weight proteinuriaAminoaciduriaHyperchloremic metabolic acidosisAbnormality of vitamin D metabolismAbnormal cornea morphologyPigmentary retinopathyAbnormality of thyroid physiologyAbnormal cerebral white matter morphologyCognitive impairment

Classification & Codes

Orphanet Code

ORPHA:411629
nephropathic infantile cystinosis
OrphanetORPHA:411629
Treatments0 drug(s)
Symptoms on record27 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO