neurodegeneration with brain iron accumulation 2A

ORPHA: 35069

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with neurodegeneration with brain iron accumulation 2A, sourced from HPO and Orphanet clinical annotations.

Cerebellar atrophyPsychomotor deteriorationDevelopmental regressionOptic atrophyAbnormality of visual evoked potentialsAtaxiaMental deteriorationSpastic tetraparesisHyperreflexiaProgressive spasticityUnsteady gaitEye of the tiger anomaly of globus pallidusBulbar signsAbnormal cerebral white matter morphologyAbnormality of peripheral nerve conductionDiffuse axonal swellingEMG: chronic denervation signsPeripheral axonal neuropathySensorimotor neuropathyAbnormal pyramidal signAxial hypotoniaPeripheral neuropathyIron accumulation in brainCerebellar gliosisIncreased circulating lactate dehydrogenase concentrationStrabismusBlindnessNystagmusAtypical behaviorEmotional labilityAutistic behaviorShort attention spanDelayed speech and language developmentHyperactivitySpasticityDysarthriaGait disturbanceDystoniaFlexion contractureConstipationDroolingTemperature instabilityAspiration pneumoniaPendular nystagmusAbnormal autonomic nervous system physiologyImpulsivitySeizureApneic episodes in infancyDownbeat nystagmusUpgaze palsyChoking episodesVegetative state

Classification & Codes

Orphanet Code

ORPHA:35069
neurodegeneration with brain iron accumulation 2A
OrphanetORPHA:35069
Treatments0 drug(s)
Symptoms on record52 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO