neurodegeneration with brain iron accumulation 4

ORPHA: 289560

Overview

neurodegeneration with brain iron accumulation that has material basis in autosomal recessive inheritance of mutation in the C19orf12 gene on chromosome 19q12

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with neurodegeneration with brain iron accumulation 4, sourced from HPO and Orphanet clinical annotations.

Atypical behaviorSpasticityDysarthriaMental deteriorationMuscle weaknessRigidityPostural instabilityHand tremorBabinski signUrinary incontinenceOptic atrophyGait disturbanceParkinsonismDystoniaDysphagiaBradykinesiaSpastic paraparesisFrequent fallsAbnormal globus pallidus morphologyBowel incontinenceHyperactive deep tendon reflexesMotor axonal neuropathyAbnormal substantia nigra morphologyAbnormal saccadic eye movementsShuffling gaitRespiratory insufficiency

Classification & Codes

Orphanet Code

ORPHA:289560
neurodegeneration with brain iron accumulation 4
OrphanetORPHA:289560
Treatments0 drug(s)
Symptoms on record26 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
neurodegeneration with brain iron accumulation 4 | OrphanDrug