neurodevelopmental disorder-craniofacial dysmorphism-cardiac defect-hip dysplasia syndrome due to a point mutation

ORPHA: 453504

Overview

human disease

Available Treatments (0)

No treatments linked yet

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Clinical Presentation

Signs and symptoms associated with neurodevelopmental disorder-craniofacial dysmorphism-cardiac defect-hip dysplasia syndrome due to a point mutation, sourced from HPO and Orphanet clinical annotations.

Severe intellectual disabilityIncreased nuchal translucencyDelayed ability to walkCleft palateBifid uvulaCoarse facial featuresConductive hearing impairmentSensorineural hearing impairmentProtruding earUnderdeveloped nasal alaeCystic hygromaPtosisHypermetropiaMyopiaShallow orbitsAbnormal optic nerve morphologyColobomaOptic nerve hypoplasiaHypothyroidismOsteopeniaHyperhidrosisSeizureAgenesis of corpus callosumAreflexiaReduced tendon reflexesMuscle weaknessJoint hypermobilityOvergrowthAtrial septal defectBicuspid aortic valveTalipes equinovarusPes planusRecurrent feverConstipationHeat intoleranceHypoplasia of the corpus callosumExaggerated cupid's bowSupernumerary nippleEpisodic vomitingGastroparesisGastrointestinal dysmotilityHigh, narrow palateNocturnal hypoventilationInverted nipplesEasy fatigabilityVertebral segmentation defectIntestinal pseudo-obstructionSagittal craniosynostosisLambdoidal craniosynostosisPreauricular pitAortic aneurysmProminent metopic ridgeAbnormality of primary teethImpaired pain sensationEversion of lateral third of lower eyelidsFeeding difficulties in infancyBranchial anomalyTooth agenesisBifid tongueOpen biteTypical absence seizureMetopic synostosisNasogastric tube feeding in infancyType 1 muscle fiber atrophyPostaxial polydactylyLong palpebral fissureHypotoniaCryptorchidismVesicoureteral refluxHydronephrosisMacroglossiaOpen mouthMicrocephalyLong faceWide nasal bridgeBroad nasal tipDental malocclusionCraniosynostosisHip dysplasiaGrowth delayAbnormal heart morphologyVentricular septal defectGray matter heterotopiaModerate intellectual disabilityPoor speechInability to walkScoliosisExaggerated median tongue furrowDownturned corners of mouthBruxism

Classification & Codes

Orphanet Code

ORPHA:453504
neurodevelopmental disorder-craniofacial dysmorphism-cardiac defect-hip dysplasia syndrome due to a point mutation
OrphanetORPHA:453504
Treatments0 drug(s)
Symptoms on record90 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO