neuronal ceroid lipofuscinosis 11
ORPHA: 3146291 Treatment Available
Overview
human disease
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| cerliponase alfa Orphan Cold Chain | intracerebroventricular infusion, 150mg/5mL | FDA Approved, EMA Approved | 8 | 30d |
Classification & Codes
Orphanet Code
ORPHA:314629neuronal ceroid lipofuscinosis 11
| Orphanet | ORPHA:314629 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO