neutral lipid storage myopathy

ORPHA: 98908

Overview

human disease

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with neutral lipid storage myopathy, sourced from HPO and Orphanet clinical annotations.

Gait disturbanceCholecystitisPineal cystShoulder girdle muscle weaknessProgressive proximal muscle weaknessIncreased intramyocellular lipid dropletsFatty replacement of skeletal muscleMotor delayGeneralized hypotoniaHepatic steatosisCardiomyopathyHypertriglyceridemiaFasciculationsElevated circulating hepatic transaminase concentrationMyopathyMyalgiaEasy fatigabilityGowers signPelvic girdle muscle weaknessVery long chain fatty acid accumulationDifficulty runningIncreased circulating lactate dehydrogenase concentrationAbnormal circulating creatine kinase concentrationSensorineural hearing impairmentNeck muscle weaknessDiabetes mellitusMild intellectual disabilityAreflexiaCongestive heart failureHepatomegalyRimmed vacuolesShort statureChronic pancreatitisFoot dorsiflexor weaknessGeneralized limb muscle atrophyProgressive distal muscle weaknessHand muscle weakness

Classification & Codes

Orphanet Code

ORPHA:98908
neutral lipid storage myopathy
OrphanetORPHA:98908
Treatments0 drug(s)
Symptoms on record37 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO