night blindness-skeletal anomalies-dysmorphism syndrome

ORPHA: 1390

Overview

This syndrome is characterized by night blindness, skeletal abnormalities (sloping shoulders, joint hyperextensibility, minor radiological anomalies) and characteristic facies (periorbital anomalies, malar flatness, retrognathia)

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with night blindness-skeletal anomalies-dysmorphism syndrome, sourced from HPO and Orphanet clinical annotations.

Joint hypermobilityAbnormal palate morphologyMalar flatteningRetrognathiaEpicanthusPtosisAbnormal electroretinogramMyopiaNyctalopiaSynophrysCarious teethBrachydactylyAbnormal retinal vascular morphologyDown-sloping shouldersAbnormality of the noseDownslanted palpebral fissuresHeterochromia iridisHypertoniaScoliosisClinodactyly of the 5th fingerAbnormal retinal pigmentationCognitive impairmentPosteriorly rotated ears

Classification & Codes

Orphanet Code

ORPHA:1390
night blindness-skeletal anomalies-dysmorphism syndrome
OrphanetORPHA:1390
Treatments0 drug(s)
Symptoms on record23 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO