Noonan syndrome and Noonan-related syndrome
ORPHA: 987331 Treatment Available
Overview
human disease
Available Treatments (1)
| Drug | Form | Status | Countries | Lead Time |
|---|---|---|---|---|
| Everolimus Orphan | Oral tablet | FDA Approved | 5 | — |
Classification & Codes
Orphanet Code
ORPHA:98733Noonan syndrome and Noonan-related syndrome
| Orphanet | ORPHA:98733 |
| Treatments | 1 drug(s) |
| Status | published |
Treatment Summary
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO