osteoporosis-pseudoglioma syndrome

MeSH: C536063ORPHA: 2788

Overview

Osteoporosis pseudoglioma syndrome is a very rare autosomal recessive disorder characterized by congenital or infancy-onset blindness and severe juvenile-onset osteoporosis and spontaneous fractures

Available Treatments (0)

No treatments linked yet

Clinical trials or compassionate use may be available — consult a specialist.

Clinical Presentation

Signs and symptoms associated with osteoporosis-pseudoglioma syndrome, sourced from HPO and Orphanet clinical annotations.

Joint hypermobilityOsteoporosisIncreased susceptibility to fracturesRetinal detachmentOsteopeniaSeverely reduced visual acuityLoss of ambulationWaddling gaitMetaphyseal wideningAbnormal vitreous humor morphologyCrumpled long bonesCongenital blindnessSerous retinal detachmentCorneal opacityFloppy infantLow serum calcitriolAngle closure glaucomaExudative vitreoretinopathyAbnormal lower limb bone morphologyMicrophthalmiaDelayed speech and language developmentGlobal developmental delayFrontal bossingDelayed gross motor developmentWormian bonesAbnormal femoral neck/head morphologyShort statureCongenital nystagmusVisual acuity light perception with projectionPreauricular skin tagBlue scleraeIsosexual precocious pubertyModerately reduced visual acuityAbnormal cardiovascular system morphology

Classification & Codes

MeSH Code

C536063

Orphanet Code

ORPHA:2788
osteoporosis-pseudoglioma syndrome
MeSHC536063
OrphanetORPHA:2788
Treatments0 drug(s)
Symptoms on record34 signs
Statuspublished
Factual Authority
Last Updated3/20/2026
Clinical DataHPO · Orphanet
Drug DataFDA · EMA · CDSCO
osteoporosis-pseudoglioma syndrome | OrphanDrug